![\"Picture](\"https:\/\/blogs.otago.ac.nz\/thesheet\/files\/2025\/10\/photo-of-brad-timms-who-has-batten-disease-sitting-in-a-wheelchair-in-a-garden-and-smiling-664226.png\")
<\/figure>What is Batten disease?<\/a><\/h3>\n<\/div><\/div>\n\n\n\n![\"Cropped](\"https:\/\/blogs.otago.ac.nz\/thesheet\/files\/2025\/10\/cropped-picture-of-a-protein-depicted-in-cartoon-format-669674.png\")
<\/figure>\nWhat causes Batten disease?<\/a><\/h3>\n<\/div><\/div>\n\n\n\n![\"Cropped](\"https:\/\/blogs.otago.ac.nz\/thesheet\/files\/2025\/10\/cropped-section-from-a-picture-of-a-family-tree-669673.png\")
<\/figure>\nRecessive genetic disorders, family trees, and genetic testing<\/a><\/h3>\n<\/div><\/div>\n\n\n\n![\"Drawing](\"https:\/\/blogs.otago.ac.nz\/thesheet\/files\/2025\/10\/gene-therapy-syringe_186-682592.png\")
<\/figure>\nGene therapy – a cure for Batten disease?<\/a><\/h3>\n<\/div><\/div>\n\n\n\n![\"Close-up](\"https:\/\/blogs.otago.ac.nz\/thesheet\/files\/2025\/10\/close-up-photo-of-a-sheeps-face-664228.jpg\")
<\/figure>\nTesting gene therapy for Batten disease in sheep<\/a><\/h3>\n<\/div><\/div>\n\n\n\n![\"Illustration](\"https:\/\/blogs.otago.ac.nz\/thesheet\/files\/2025\/10\/silhouettes-question-mark_186-683021.jpg\")
<\/figure>\nBiological implications of gene therapy<\/a><\/h3>\n<\/div><\/div>\n\n\n\nMore information on Batten disease and gene therapy:<\/p>\n\n\n\n
\n- Lysosomal Diseases New Zealand<\/a><\/li>\n\n\n\n
- Batten Disease Support and Research Association<\/a><\/li>\n\n\n\n
- Genes and gene therapy (U.S. National Library of Medicine)<\/a><\/li>\n<\/ul>\n\n\n\n
\n\n\n\nOther useful links:<\/p>\n\n\n\n
\n- Otago Biochemistry school resources<\/a><\/li>\n\n\n\n
- Otago Biochemistry website<\/a><\/li>\n<\/ul>\n\n\n\n
<\/p>\n","protected":false},"excerpt":{"rendered":"
Genetic transfer in medicine: Batten disease Inheriting small mutations can sometimes have devastating effects on people’s lives. Otago Department of Biochemistry researcher Dr Stephanie Hughes and her research team study a rare genetic neurodegenerative disorder called Batten disease. They are […]<\/p>\n","protected":false},"author":32571,"featured_media":0,"parent":3950,"menu_order":2,"comment_status":"closed","ping_status":"closed","template":"","meta":{"footnotes":""},"class_list":["post-4002","page","type-page","status-publish","hentry"],"_links":{"self":[{"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/pages\/4002","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/pages"}],"about":[{"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/types\/page"}],"author":[{"embeddable":true,"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/users\/32571"}],"replies":[{"embeddable":true,"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/comments?post=4002"}],"version-history":[{"count":0,"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/pages\/4002\/revisions"}],"up":[{"embeddable":true,"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/pages\/3950"}],"wp:attachment":[{"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/media?parent=4002"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}
<\/figure>What causes Batten disease?<\/a><\/h3>\n<\/div><\/div>\n\n\n\n<\/figure>\nRecessive genetic disorders, family trees, and genetic testing<\/a><\/h3>\n<\/div><\/div>\n\n\n\n<\/figure>\nGene therapy – a cure for Batten disease?<\/a><\/h3>\n<\/div><\/div>\n\n\n\n<\/figure>\nTesting gene therapy for Batten disease in sheep<\/a><\/h3>\n<\/div><\/div>\n\n\n\n<\/figure>\nBiological implications of gene therapy<\/a><\/h3>\n<\/div><\/div>\n\n\n\nMore information on Batten disease and gene therapy:<\/p>\n\n\n\n
\n- Lysosomal Diseases New Zealand<\/a><\/li>\n\n\n\n
- Batten Disease Support and Research Association<\/a><\/li>\n\n\n\n
- Genes and gene therapy (U.S. National Library of Medicine)<\/a><\/li>\n<\/ul>\n\n\n\n
\n\n\n\nOther useful links:<\/p>\n\n\n\n
\n- Otago Biochemistry school resources<\/a><\/li>\n\n\n\n
- Otago Biochemistry website<\/a><\/li>\n<\/ul>\n\n\n\n
<\/p>\n","protected":false},"excerpt":{"rendered":"
Genetic transfer in medicine: Batten disease Inheriting small mutations can sometimes have devastating effects on people’s lives. Otago Department of Biochemistry researcher Dr Stephanie Hughes and her research team study a rare genetic neurodegenerative disorder called Batten disease. They are […]<\/p>\n","protected":false},"author":32571,"featured_media":0,"parent":3950,"menu_order":2,"comment_status":"closed","ping_status":"closed","template":"","meta":{"footnotes":""},"class_list":["post-4002","page","type-page","status-publish","hentry"],"_links":{"self":[{"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/pages\/4002","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/pages"}],"about":[{"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/types\/page"}],"author":[{"embeddable":true,"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/users\/32571"}],"replies":[{"embeddable":true,"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/comments?post=4002"}],"version-history":[{"count":0,"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/pages\/4002\/revisions"}],"up":[{"embeddable":true,"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/pages\/3950"}],"wp:attachment":[{"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/media?parent=4002"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}
<\/figure>Recessive genetic disorders, family trees, and genetic testing<\/a><\/h3>\n<\/div><\/div>\n\n\n\n<\/figure>\nGene therapy – a cure for Batten disease?<\/a><\/h3>\n<\/div><\/div>\n\n\n\n<\/figure>\nTesting gene therapy for Batten disease in sheep<\/a><\/h3>\n<\/div><\/div>\n\n\n\n<\/figure>\nBiological implications of gene therapy<\/a><\/h3>\n<\/div><\/div>\n\n\n\nMore information on Batten disease and gene therapy:<\/p>\n\n\n\n
\n- Lysosomal Diseases New Zealand<\/a><\/li>\n\n\n\n
- Batten Disease Support and Research Association<\/a><\/li>\n\n\n\n
- Genes and gene therapy (U.S. National Library of Medicine)<\/a><\/li>\n<\/ul>\n\n\n\n
\n\n\n\nOther useful links:<\/p>\n\n\n\n
\n- Otago Biochemistry school resources<\/a><\/li>\n\n\n\n
- Otago Biochemistry website<\/a><\/li>\n<\/ul>\n\n\n\n
<\/p>\n","protected":false},"excerpt":{"rendered":"
Genetic transfer in medicine: Batten disease Inheriting small mutations can sometimes have devastating effects on people’s lives. Otago Department of Biochemistry researcher Dr Stephanie Hughes and her research team study a rare genetic neurodegenerative disorder called Batten disease. They are […]<\/p>\n","protected":false},"author":32571,"featured_media":0,"parent":3950,"menu_order":2,"comment_status":"closed","ping_status":"closed","template":"","meta":{"footnotes":""},"class_list":["post-4002","page","type-page","status-publish","hentry"],"_links":{"self":[{"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/pages\/4002","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/pages"}],"about":[{"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/types\/page"}],"author":[{"embeddable":true,"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/users\/32571"}],"replies":[{"embeddable":true,"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/comments?post=4002"}],"version-history":[{"count":0,"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/pages\/4002\/revisions"}],"up":[{"embeddable":true,"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/pages\/3950"}],"wp:attachment":[{"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/media?parent=4002"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}
<\/figure>Gene therapy – a cure for Batten disease?<\/a><\/h3>\n<\/div><\/div>\n\n\n\n<\/figure>\nTesting gene therapy for Batten disease in sheep<\/a><\/h3>\n<\/div><\/div>\n\n\n\n<\/figure>\nBiological implications of gene therapy<\/a><\/h3>\n<\/div><\/div>\n\n\n\nMore information on Batten disease and gene therapy:<\/p>\n\n\n\n
\n- Lysosomal Diseases New Zealand<\/a><\/li>\n\n\n\n
- Batten Disease Support and Research Association<\/a><\/li>\n\n\n\n
- Genes and gene therapy (U.S. National Library of Medicine)<\/a><\/li>\n<\/ul>\n\n\n\n
\n\n\n\nOther useful links:<\/p>\n\n\n\n
\n- Otago Biochemistry school resources<\/a><\/li>\n\n\n\n
- Otago Biochemistry website<\/a><\/li>\n<\/ul>\n\n\n\n
<\/p>\n","protected":false},"excerpt":{"rendered":"
Genetic transfer in medicine: Batten disease Inheriting small mutations can sometimes have devastating effects on people’s lives. Otago Department of Biochemistry researcher Dr Stephanie Hughes and her research team study a rare genetic neurodegenerative disorder called Batten disease. They are […]<\/p>\n","protected":false},"author":32571,"featured_media":0,"parent":3950,"menu_order":2,"comment_status":"closed","ping_status":"closed","template":"","meta":{"footnotes":""},"class_list":["post-4002","page","type-page","status-publish","hentry"],"_links":{"self":[{"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/pages\/4002","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/pages"}],"about":[{"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/types\/page"}],"author":[{"embeddable":true,"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/users\/32571"}],"replies":[{"embeddable":true,"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/comments?post=4002"}],"version-history":[{"count":0,"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/pages\/4002\/revisions"}],"up":[{"embeddable":true,"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/pages\/3950"}],"wp:attachment":[{"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/media?parent=4002"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}
<\/figure>Testing gene therapy for Batten disease in sheep<\/a><\/h3>\n<\/div><\/div>\n\n\n\n<\/figure>\nBiological implications of gene therapy<\/a><\/h3>\n<\/div><\/div>\n\n\n\nMore information on Batten disease and gene therapy:<\/p>\n\n\n\n
\n- Lysosomal Diseases New Zealand<\/a><\/li>\n\n\n\n
- Batten Disease Support and Research Association<\/a><\/li>\n\n\n\n
- Genes and gene therapy (U.S. National Library of Medicine)<\/a><\/li>\n<\/ul>\n\n\n\n
\n\n\n\nOther useful links:<\/p>\n\n\n\n
\n- Otago Biochemistry school resources<\/a><\/li>\n\n\n\n
- Otago Biochemistry website<\/a><\/li>\n<\/ul>\n\n\n\n
<\/p>\n","protected":false},"excerpt":{"rendered":"
Genetic transfer in medicine: Batten disease Inheriting small mutations can sometimes have devastating effects on people’s lives. Otago Department of Biochemistry researcher Dr Stephanie Hughes and her research team study a rare genetic neurodegenerative disorder called Batten disease. They are […]<\/p>\n","protected":false},"author":32571,"featured_media":0,"parent":3950,"menu_order":2,"comment_status":"closed","ping_status":"closed","template":"","meta":{"footnotes":""},"class_list":["post-4002","page","type-page","status-publish","hentry"],"_links":{"self":[{"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/pages\/4002","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/pages"}],"about":[{"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/types\/page"}],"author":[{"embeddable":true,"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/users\/32571"}],"replies":[{"embeddable":true,"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/comments?post=4002"}],"version-history":[{"count":0,"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/pages\/4002\/revisions"}],"up":[{"embeddable":true,"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/pages\/3950"}],"wp:attachment":[{"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/media?parent=4002"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}
<\/figure>Biological implications of gene therapy<\/a><\/h3>\n<\/div><\/div>\n\n\n\nMore information on Batten disease and gene therapy:<\/p>\n\n\n\n
\n- Lysosomal Diseases New Zealand<\/a><\/li>\n\n\n\n
- Batten Disease Support and Research Association<\/a><\/li>\n\n\n\n
- Genes and gene therapy (U.S. National Library of Medicine)<\/a><\/li>\n<\/ul>\n\n\n\n
\n\n\n\nOther useful links:<\/p>\n\n\n\n
\n- Otago Biochemistry school resources<\/a><\/li>\n\n\n\n
- Otago Biochemistry website<\/a><\/li>\n<\/ul>\n\n\n\n
<\/p>\n","protected":false},"excerpt":{"rendered":"
Genetic transfer in medicine: Batten disease Inheriting small mutations can sometimes have devastating effects on people’s lives. Otago Department of Biochemistry researcher Dr Stephanie Hughes and her research team study a rare genetic neurodegenerative disorder called Batten disease. They are […]<\/p>\n","protected":false},"author":32571,"featured_media":0,"parent":3950,"menu_order":2,"comment_status":"closed","ping_status":"closed","template":"","meta":{"footnotes":""},"class_list":["post-4002","page","type-page","status-publish","hentry"],"_links":{"self":[{"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/pages\/4002","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/pages"}],"about":[{"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/types\/page"}],"author":[{"embeddable":true,"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/users\/32571"}],"replies":[{"embeddable":true,"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/comments?post=4002"}],"version-history":[{"count":0,"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/pages\/4002\/revisions"}],"up":[{"embeddable":true,"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/pages\/3950"}],"wp:attachment":[{"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/media?parent=4002"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}
\n\n\n\n
Other useful links:<\/p>\n\n\n\n
- \n
- Otago Biochemistry school resources<\/a><\/li>\n\n\n\n
- Otago Biochemistry website<\/a><\/li>\n<\/ul>\n\n\n\n
<\/p>\n","protected":false},"excerpt":{"rendered":"
Genetic transfer in medicine: Batten disease Inheriting small mutations can sometimes have devastating effects on people’s lives. Otago Department of Biochemistry researcher Dr Stephanie Hughes and her research team study a rare genetic neurodegenerative disorder called Batten disease. They are […]<\/p>\n","protected":false},"author":32571,"featured_media":0,"parent":3950,"menu_order":2,"comment_status":"closed","ping_status":"closed","template":"","meta":{"footnotes":""},"class_list":["post-4002","page","type-page","status-publish","hentry"],"_links":{"self":[{"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/pages\/4002","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/pages"}],"about":[{"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/types\/page"}],"author":[{"embeddable":true,"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/users\/32571"}],"replies":[{"embeddable":true,"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/comments?post=4002"}],"version-history":[{"count":0,"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/pages\/4002\/revisions"}],"up":[{"embeddable":true,"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/pages\/3950"}],"wp:attachment":[{"href":"https:\/\/blogs.otago.ac.nz\/thesheet\/wp-json\/wp\/v2\/media?parent=4002"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}
- Otago Biochemistry website<\/a><\/li>\n<\/ul>\n\n\n\n